Written Question·Department of Health and Social Care·UIN 86757

Rare Diseases: Medical Treatments

Tabled: 30 October 2025
Answered: 10 November 2025

Question

Claire Hanna

Social Democratic & Labour PartyBelfast South and Mid Down

To ask the Secretary of State for Health and Social Care, what assessment his Department has made of the adequacy of appraisal processes for (a) Freidrich’s Ataxia, (b) Neiman Pick’s disease and (c) other rare diseases for exceptional conditions.

Answer

Dr Zubir Ahmed
The National Institute for Health and Care Excellence’s (NICE) methods have been proven to be suitable for the evaluation of rare disease medicines, where companies are willing to price their medicines fairly. NICE’s approval rate for medicines for rare d...

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